The rejection of Disc Medicine Inc.’s experimental compound for a rare and devastating disorder by the US Food and Drug Administration, just months after it received a voucher intended to speed US ...

By Sneha S K Feb 13 (Reuters) - Disc Medicine said on Friday the U.S. Food and Drug Administration declined to approve its drug to treat a rare genetic disorder. The drug, bitopertin, was being ...

Leena Panwala and Tim Drury share their stories with "CBS Mornings" about how they're raising awareness and money for INAD, a rare genetic disorder. Panwala created the INAD Cure foundation after her ...

A new study has brought scientists one step further in the direction of developing a cure for a brutal group of rare brain disorders known as SYNGAP1-related disorders, or SRDs. Researchers were able ...

Faced with a life-threatening metabolic disease, KJ’s doctors at Children’s Hospital of Philadelphia sprinted to create a ...

The idea of self-amplifying gene editing is to get cells to pass on packages of CRISPR machinery to their neighbours, boosting the effect ...

Genetic testing can help doctors diagnose some neurological disorders, such as Huntington’s disease. It can also provide insights into a person’s risk of future health conditions. Genetic testing ...

About 1 in 4 people suffer from an anxiety disorder at some point in their lives. These include panic disorder with sudden, severe anxiety attacks; generalized anxiety disorder, in which sufferers ...

By Bhanvi Satija LONDON, Feb 2 (Reuters) - French drugmaker Sanofi said on Monday that its experimental genetic disorder ...

HOSPITAL staff have been told by officials to stop discouraging first-cousin marriages despite the increased risk of birth ...

By Dr. Priyom Bose, Ph.D. A sweeping genetic analysis reveals when obesity is the common thread linking chronic diseases, and when other biology is to blame. Study: Genetics identifies obesity as a ...

Despite widespread misconceptions, eating disorders aren't a choice, they're serious, potentially life-threatening conditions. While social and environmental factors do influence someone's risk of ...